Webinars
13 March 2026 - 13 May 2026
Webinar: Orphan Drug Status: Regulatory Approaches and Practices of EAEU Countries
26 February 2026
Webinar "MCDA for Policy Making on Orphan Medicinal Products (OMPs)
02 December 2025
Webinar "Management of Hemophilia as a Rare Disease: Models for Accessing Innovative Therapies" Türkiye
22 October 2025
Webinar "Multi-Criteria Decision Analysis (MCDA) in Rare Diseases"
18 April 2025
Webinar "Real world evidence and real world data (RWE/RWD) in rare diseases"
News
Saudi Arabia is introducing a new accelerated route for orphan drugs.
FDA Proposes to Reduce Regulatory Burden in the Development of Platform-Based Gene Therapy Using Genome Editing
Patient Organisations in Europe Submit Comments on the First Joint Clinical Assessment Report under the HTA Regulation