News
FDA relaxes requirements for manufacturing cell and gene therapies in clinical development
Changes to the list of orphan diseases and drugs have come into force in Kazakhstan
HAS (France) analyzed the use of real-world clinical practice data in clinical and economic studies of innovative technologies
Personalized CRISPR therapy for CPS1 deficiency: Clinical results of the world's first case
UHC in the CIS countries: key figures and the meaning behind them
December 12 is Universal Health Coverage Day.
Gene-cell therapies in the sights of HTA: An international study has shown that the success of high-tech drugs (HTDs) is determined not only by price
EMA recommends approval of Waskyra, a gene therapy treatment for Wiskott-Aldrich syndrome
The Organization for Rare Diseases of India (ORDI) is calling for funding for rare diseases based on the Russian "Circle of Good" model.
WHO has released guidelines on best practices for conducting clinical trials: what trials should look like today
FDA approves first gene replacement therapy for SMA available to all ages
Uzbekistan: New state program to help children with orphan diseases for 2026–2030
The CIS Orphan Consortium has a new member!
Europe strengthens partnerships for rare disease research
MCDA in Rare Diseases: A Tool for Accurate and Fair Treatment Evaluation
Kazakhstan: Medicines and Innovative Technologies – Experience and Prospects
Orphan diseases and pediatric anesthesiology: the experience of Russia and Uzbekistan
RWE in Orphan Diseases: International Dialogue and Joint Decisions
Biomedical Collaboration: A Visit to Beijing's Daxing Science and Technology Park
Visit of NAERES representatives to the Beijing Orphan Center
A cooperation agreement was signed between the National Medical Chamber of Russia and the Chinese Medical Association.