News
December 12 is Universal Health Coverage Day.
Gene-cell therapies in the sights of HTA: An international study has shown that the success of high-tech drugs (HTDs) is determined not only by price
EMA recommends approval of Waskyra, a gene therapy treatment for Wiskott-Aldrich syndrome
The Organization for Rare Diseases of India (ORDI) is calling for funding for rare diseases based on the Russian "Circle of Good" model.
WHO has released guidelines on best practices for conducting clinical trials: what trials should look like today
FDA approves first gene replacement therapy for SMA available to all ages
Uzbekistan: New state program to help children with orphan diseases for 2026–2030
The CIS Orphan Consortium has a new member!
MCDA in Rare Diseases: A Tool for Accurate and Fair Treatment Evaluation
Orphan diseases and pediatric anesthesiology: the experience of Russia and Uzbekistan
RWE in Orphan Diseases: International Dialogue and Joint Decisions
Biomedical Collaboration: A Visit to Beijing's Daxing Science and Technology Park
Visit of NAERES representatives to the Beijing Orphan Center
A cooperation agreement was signed between the National Medical Chamber of Russia and the Chinese Medical Association.
Orphan Center of Morozov Hospital: 10 years of systematic assistance to children with rare diseases in Moscow
Russia: Orphan Center of Moscow Region
Orphan centers are a key element in the system of care for patients with rare diseases
SMA: Russia's path from emergency response to a systemic model of care